Genetic diagnosis Rett syndrome: a first step to drug therapy. Study on the involved and genes genotype-phenotype correlation

Reference:
Armstrong

Abstract:
Determine the pathogenicity of the mutations and polymorphisms detected in genes MECP2, CDKL5, FOXG1, NTNG1 i BDNF responsible for RTT in all patients clinically diagnosed as RTT and determine the clinical expression in patients (genotype-phenotype correlation). Objectives: – To study the genotype of patients with RTT you have not found a point mutation in exons 3 and 4, or large gene MECP2 gene rearrangement. Search for mutations in CDKL5 and FOXG1 genes in atypical RTT variant with early epilepsy and congenital form respectively – To study the phenotype of patients with the items listed in the database used specifically for the RTT; define its (classical or variant) clinically determine the clinical severity using our check-list of disability – To correlate phenotype to genotype in order to offer a forecast clinical and family and prenatal advice.

PROJECT DETAILS 

beginning: 2010.

end: 2012.

Country of research: Spain

Counry of funding source: Spain

Funding organization: Fondo Biorett

Financing: PRIVATE FUNDERS – 310 844 €

hyperlink

By continuing to use the site, you agree to the use of cookies. more information

The cookie settings on this website are set to "allow cookies" to give you the best browsing experience possible. If you continue to use this website without changing your cookie settings or you click "Accept" below then you are consenting to this.

Close